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In December 2023, the U.S. Food and Drug Administration approved two new therapies, the first cell-based gene therapies for the treatment of sickle cell disease. Learn more here and check back for new and updated resources.
ABOUT CURESCI
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SICKLE CELL DISEASE
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Cure Sickle Cell Initiative Information
CureSCi Patient Engagement Journey
FROM CURESCI
It's Time to Rewrite the Story of Sickle Cell.
An Introduction to CureSci Webinar
Held on September 11, 2019
FROM CURESCI
Cure Sickle Cell Initiative Patient Brochure
EN ESPAÑOL
Sickle Cell Disease Information
National Heart, Lung, and Blood Institute (NHLBI): Health Topics – Sickle Cell Disease
ASH/CDC: Steps to Better Health for People with Sickle Cell Disease Toolkit
National Human Genome Research Institute (NHGRI): About Sickle Cell Disease
U.S. National Library of Medicine: Sickle Cell Disease
Genetic Therapies Information
Get to Know Gene Therapies for Sickle Cell Disease
National Heart, Lung, and Blood Institute (NHLBI)
National Heart, Lung, and Blood Institute (NHLBI): Genome Editing for Sickle Cell Disease
National Library of Medicine (NLM)
Gene Therapy Education Materials for the Sickle Cell Disease Community
American Society of Gene & Cell Therapy (ASGCT) - Video
How Gene Therapy Can Cure or Treat Diseases
US Food & Drug Administration: Gene Therapy Inside Out
American Society of Gene & Cell Therapy (ASGCT) - Gene Therapy Basics
American Society of Gene & Cell Therapy (ASGCT): Sickle Cell Disease Treatments
National Organization for Rare Disorders: Gene Therapy – Your Questions Answered
Hope for a Cure: Treating Sickle Cell Disease with CRISPR
American Society of Gene & Cell Therapy (ASGCT) - Webinars
Boston Children's Hospital: How Ex-Vivo Gene Therapy Works
Clinical Trial Resources
NHLBI Health Topics: Clinical Trials
NIH Clinical Research Trials and You
U.S. Food and Drug Administration: Clinical Trials-What Patients Need to Know
ClinicalTrials.gov
ASH Research Collaborative: Why Participate in Clinical Trials for Sickle Cell Disease?
CISCRP Participant Bill of Rights
CISCRP Questions to Ask
CureSCi Resources
FROM CURESCI
Clinical Trials Listing Handout
FROM CURESCI
Gene Therapies Webinar
Held on September 11, 2019
FROM CURESCI
How Can Gene Therapy Cure Sickle Cell Disease? (Infographic)
FROM CURESCI
Conditioning Fact Sheet for Patients