Dr. Traci Mondoro

Working Together as
a Community

The Cure Sickle Cell Initiative includes people from various scientific disciplines—basic and clinical researchers, statisticians, data scientists, geneticists, clinical trialists, and others who are actively involved in various sub-committees and working groups. An important element of the Initiative is working together as a community to accelerate research by avoiding duplication of efforts, leveraging evolving knowledge, and integrating best practices from government, academia, and industry.

Current efforts focus on six key priorities: creating biological and clinical endpoints, developing data resources, enhancing existing bio resources, engaging patients through outreach, designing a regulatory interface, and enabling and accelerating clinical trials.

Gene therapy could be life-changing for patients with sickle cell disease and give them a whole new way of living and way to think about life.

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NHLBI AND GENE THERAPY RESEARCH